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Titin mutation segregates with hereditary myopathy with early respiratory failure

  • Gerald Pfeffer
  • , Hannah R Elliott
  • , Helen Griffin
  • , Rita Barresi
  • , James Miller
  • , Julie Marsh
  • , Anni Evilä
  • , Anna Vihola
  • , Peter Hackman
  • , Volker Straub
  • , David J Dick
  • , Rita Horvath
  • , Mauro Santibanez-Koref
  • , Bjarne Udd
  • , Patrick F Chinnery

    Research output: Contribution to journalArticleScientificpeer-review

    126 Citations (Scopus)
    Original languageEnglish
    Pages (from-to)1695-1713
    JournalBrain
    Volume135
    Issue number6
    DOIs
    Publication statusPublished - 2012
    Publication typeA1 Journal article-refereed

    Keywords

    • cytoplasmic body
    • distal myopathy
    • exome sequencing
    • hereditary myopathy with early respiratory failure
    • titin

    Publication forum classification

    • Publication forum level 3

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